Haematology: clinical-trial pipeline

11,099 haematology trials are in ClinicalTrials.gov and the EU CTIS portal; 2,534 are not yet finished and 332 of those are in phase 2/3 or 3. Source: Arcadium Data, data as of .

Open trials by phase

PhaseTrials
Not applicable1,153
Phase 2464
Phase 3288
Phase 1209
Phase 1/2198
Phase 4129
Early phase 149
Phase 2/344

Sponsors with the most open trials

SponsorTypeOpen trialsPhase 3Countries
Institute of Hematology & Blood Diseases Hospital, Chinaacademic7612
Assiut Universityacademic50310
M.D. Anderson Cancer Centeracademic48134
Assistance Publique - Hôpitaux de Parisacademic44826
National Cancer Institute (NCI)government44276
National Heart, Lung, and Blood Institute (NHLBI)government29013
St. Jude Children's Research Hospitalacademic26021
Children's Hospital Medical Center, Cincinnatiacademic20024
Peking University People's Hospitalacademic1921
Celgeneindustry19876
Novartis Pharmaceuticalsindustry18899
City of Hope Medical Centeracademic18111
Novo Nordisk A/Sindustry17879
Sohag Universityacademic1605
Memorial Sloan Kettering Cancer Centeracademic14124
Regeneron Pharmaceuticalsindustry14659
Pfizerindustry139100
Takedaindustry13673
Peking Union Medical College Hospitalacademic1322
AstraZenecaindustry13592
Gruppo Italiano Malattie EMatologiche dell'Adultoother13321
The First Affiliated Hospital of Soochow Universityacademic1321
Agios Pharmaceuticals, Inc.industry13832
Sanofiindustry127105
Janssen Research & Development, LLCindustry12689

Recently changed open trials

Registry idTitleSponsorPhaseStatusCountries
2024-511651-17-00A phase II multicenter single-armed study using subject-specific minimal residual minimal disease markers to…Karolinska University HospitalPhase 2RecruitingDenmark, Finland, Norway, Sweden
2023-509019-97-00HEAT-AML (Hydroxyurea-Enhanced Ara-C Treatment of Adult Acute Myeloid Leukaemia): A phase I/II multi-centre s…Karolinska University HospitalPhase 1/2Active, not recruitingSweden
NCT06093672Study on Efficacy and Safety of Givinostat Versus Hydroxyurea in Patients With Polycythemia VeraItalfarmacoPhase 3RecruitingAustria, Bulgaria, Germany, Spain +11
2023-508212-38-00TALTEC: A phase II study measuring MRD negativity after bispecific T-cell redirectors TALquetamab and TEClist…North Estonia Medical Centre FoundationPhase 2Active, not recruitingDenmark, Estonia, Norway
NCT04657822Rollover Study for Patients With Sickle Cell Disease Who Have Completed a Prior Novartis-Sponsored Crizanlizu…Novartis PharmaceuticalsPhase 4Active, not recruitingBelgium, Brazil, Colombia, Germany +6
NCT03793478Safety and Efficacy of Quizartinib in Children and Young Adults With Acute Myeloid Leukemia (AML), a Cancer o…Daiichi SankyoPhase 1/2Active, not recruitingBelgium, Canada, Denmark, Spain +6
NCT06716814Study to Provide Continued Access to Treatment for Patients Completing a Previous Trial With Efanesoctocog Al…Swedish Orphan BiovitrumPhase 3Active, not recruitingBulgaria, Germany, Spain, France +6
NCT06523959Avoiding Risks of Thrombosis and Bleeding in Surgery (ARTS) TrialClinical Urology and Epidemiology Working GroupPhase 4RecruitingFinland
NCT06252870Study Testing Two Conditioning Regimen With a Single Prophylaxis of GVHD by Cyclophosphamide and Methotrexate…Nantes University HospitalPhase 2RecruitingFrance
NCT05317416Study With Elranatamab Versus Lenalidomide in Patients With Newly Diagnosed Multiple Myeloma After TransplantPfizerPhase 3Active, not recruitingAustria, Australia, Belgium, Brazil +22
2024-512731-74-00Venetoclax and Dexamethasone in translocation (11;14) positive relapsed and refractory multiple myeloma (VICT…Lillebaelt HospitalPhase 2Active, not recruitingDenmark
2023-506705-20-00CARMOD - Golcadomide (BMS-986369) post-CAR T-cell in R/R Aggressive large B-cell lymphoma patients with high…Lymphoma Academic Research OrganisationPhase 2RecruitingFrance
NCT06379789A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV13…Regeneron PharmaceuticalsPhase 1/2RecruitingAustralia, Brazil, Canada, Germany +5
NCT03937154Study of Romiplostim for Chemotherapy-induced Thrombocytopenia in Adult Subjects With Non-small Cell Lung Can…AmgenPhase 3Active, not recruitingArgentina, Brazil, Spain, Greece +6
2023-510316-39-00AML-VAC-XS15-01: Multi-peptide vaccination adjuvanted with the TLR1/2 ligand XS15 in acute myeloid leukemia (…Universitaetsklinikum Tuebingen AöRPhase 1RecruitingGermany
2023-508420-36-00Phase I clinical trial on the use of fresh, allogeneic, second-generation CD19-CAR T cells for treatment of c…Ospedale Pediatrico Bambino Gesu'Phase 1RecruitingItaly
2023-508355-39-00Phase I/II study of anti-CD7 Chimeric Antigen Receptor-Expressing T cells in pediatric patients/young adult a…Ospedale Pediatrico Bambino Gesu'Phase 1/2RecruitingItaly
NCT06926205CHOP Plus Mosunetuzumab as First Line in Patients With Richter´s Syndrome: a Phase II Study of the Spanish Gr…GELLC (Grupo Español de Leucemia Linfocítica Crónica)Phase 2Active, not recruitingSpain
NCT05254743A Study of Pirtobrutinib (LOXO-305) Versus Ibrutinib in Participants With Chronic Lymphocytic Leukemia (CLL)/…Loxo Oncology, Inc.Phase 3RecruitingArgentina, Austria, Australia, Belgium +18
NCT04077307A Study in Leukemia Patients With KaronudibThomas Helleday FoundationPhase 1RecruitingDenmark, Serbia, Sweden

All areas: clinical-trial pipeline by sponsor.

Track a sponsor's pipeline

The API returns the same trials by sponsor website, phase, status, condition and country with a change feed, joined to hiring and public contract awards. Try it without a key on one sponsor.

Sources: ClinicalTrials.gov (U.S. National Library of Medicine, public domain) and the EU Clinical Trials Information System public portal (European Medicines Agency), data as of 2026-10-25. A trial that one register cites in the other is shown once. Organisation-level data only: investigators, contact persons and site names are not stored, and a sponsor that could be a private person is withheld. Sponsor-to-website matches are made by name and can be wrong; check the register before relying on a record. Independent of the NLM, NIH and EMA.

Cite as: Arcadium Data, "Haematology clinical trials: 2,534 open, 332 in phase 3", https://arcadiumdata.io/clinical-trials/area/haematology/, data as of 2026-10-25.